Adenosine Deaminase Deficiency

Also known as: ADA Deficiency / Adenosine deaminase deficiency, unspecified / Adenosine deaminase [ADA] deficiency / Adenosine deaminase deficiency (disorder) / Combined immunodeficiency, unspecified / Combined immunodeficiency / Combined immunodeficiency syndrome / Combined immunity deficiency / Combined immunodeficiencies / Combined immunodeficiency disease (disorder)

DrugDrug NameDrug Description
DB00061PegademaseA modified form of bovine adenosine deaminase used to treat adenosine deaminase deficiency, a condition which leads to the formation of adenosine metabolites which are cytotoxic to lymphocytes.
DrugDrug NamePhaseStatusCount
DB00091Cyclosporine1Completed1
DB00688Mycophenolate mofetil1Completed1
DB01008Busulfan1 / 2Completed1
DB14712Elapegademase3Completed1
DB00061Pegademase3Completed1
DB00640AdenosineNot AvailableEnrolling by Invitation1
DB14712ElapegademaseNot AvailableCompleted1