Nephropathic Cystinosis

Also known as: Cystinosis, Nephropathic / Infantile nephropathic cystinosis (disorder) / Fanconi Bickel Syndrome / Glycogenosis with glucoaminophosphaturia (disorder) / Cystinosis / Cystinosis (disorder)

DrugDrug NameDrug Description
DB00847CysteamineA cystine depleting agent used to treat the effects of cystinosis.
DrugDrug NamePhaseStatusCount
DB00847CysteamineNot AvailableCompleted1
DB00847CysteamineNot AvailableEnrolling by Invitation1