Treosulfan Recruiting Phase 2 Trials for Bone Marrow Failure Syndromes / Inborn Errors of Metabolism / Haemoglobinopathies congenital / Congenital Immunodeficiency Treatment

IndicationsStatusPurposePhase
RecruitingTreatment2
clinicaltrials.gov IdentifierTitleDrugs
NCT02349906Treosulfan-based Versus Busulfan-based Conditioning in Paediatric Patients With Non-malignant Diseases