Barth Syndrome

Also known as: 3-Methylglutaconic aciduria type 2 (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB11981Elamipretide2 / 3Completed1
DB11981ElamipretideNot AvailableAvailable1
DB11677TriheptanoinNot AvailableNo Longer Available1