Protoporphyria, Erythropoietic

Also known as: Erythropoietic Protoporphyria (EPP) / Erythropoietic Protoporphyria / Hereditary erythropoietic porphyria / Erythropoietic protoporphyria (disorder) / Ferrochelatase deficiency (disorder) / Ferrochelatase Deficiency / Porphyria non-acute

DrugDrug NameDrug Description
DB04931AfamelanotideAn injectable subcutaneous implant used to mitigate phototoxicity secondary to erythropoietic protoporphyria (EPP).
DrugDrug NamePhaseStatusCount
DB04931Afamelanotide2Completed1
DB12426Bitopertin2Active Not Recruiting1
DB00501Cimetidine2Recruiting1
DB18007Dersimelagon2Completed1
DB12426Bitopertin2 / 3Enrolling by Invitation1
DB00375Colestipol2 / 3Completed1
DB04931Afamelanotide3Completed4
DB09485Cysteine3Completed1
DB18007Dersimelagon3Recruiting1
DB09485CysteineNot AvailableCompleted1
DB13257Ferrous sulfate anhydrousNot AvailableCompleted1
DB00951IsoniazidNot AvailableTerminated1