Homocystinuria

Also known as: Homocystinuria (disorder)

DrugDrug NameDrug Description
DB06756BetaineA methyl group donor used for the treatment of homocystinuria to decrease elevated homocysteine blood levels.
DrugDrug NamePhaseStatusCount
DB17666SYNB13531Completed1
DB17677Pegtibatinase1 / 2Active Not Recruiting1
DB01956Taurine1 / 2Completed1
DB11103Taurine1 / 2Completed1
DB06151Acetylcysteine2Completed1
DB06756Betaine2Completed1
DB17677Pegtibatinase3Recruiting1