Glycogen Storage Disease Type I
Also known as: Von Gierke's disease / Glycogen Storage Disorder Type 1 / Glycogen Storage Disease Type 1 (GSD 1) / Von Gierke Disease / Type I glycogen storage disease / Glucose-6-phosphatase deficiency / Glycogen storage disease, type I (disorder) / Deficiency of glucose-6-phosphatase (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB11677 | Triheptanoin | 0 | Completed | 1 |
DB09038 | Empagliflozin | 2 | Unknown Status | 1 |