Glycogen Storage Disease Type I

Also known as: Von Gierke's disease / Glycogen Storage Disorder Type 1 / Glycogen Storage Disease Type 1 (GSD 1) / Von Gierke Disease / Type I glycogen storage disease / Glucose-6-phosphatase deficiency / Glycogen storage disease, type I (disorder) / Deficiency of glucose-6-phosphatase (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB11677Triheptanoin0Completed1
DB09038Empagliflozin2Unknown Status1