Glycogen Storage Disease Type V
Also known as: McArdle Disease / McArdles disease / Glycogenosis type V / McArdle's disease / Type V glycogen storage disease / Glycogen storage disease, type V (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB05236 | ReN001 | 1 | Completed | 1 |
DB11677 | Triheptanoin | 2 | Completed | 1 |
DB11677 | Triheptanoin | 2 | Unknown Status | 1 |
DB00313 | Valproic acid | 2 | Completed | 1 |