Mucopolysaccharidosis VI

Also known as: Mucopolysaccharidosis Type VI (MPS VI) / Maroteaux-Lamy Syndrome / Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) / Maroteaux Lamy Syndrome / Mucopolysaccharidosis Type VI / Maroteaux-Lamy syndrome (disorder) / Deficiency of N-acetylgalactosamine-4-sulfatase (disorder)

DrugDrug NameDrug Description
DB01279GalsulfaseA recombinant human enzyme used as replacement enzyme therapy for the treatment of of adults and children with Mucopolysaccharidosis VI, a rare genetic disorder caused by a deficiency of a lysosomal enzyme.
DrugDrug NamePhaseStatusCount
DB00051Adalimumab1 / 2Active Not Recruiting1
DB00051Adalimumab1 / 2Completed1
DB00087Alemtuzumab2Completed1
DB00087Alemtuzumab2Terminated1
DB00098Antithymocyte immunoglobulin (rabbit)2Completed1
DB01008Busulfan2Completed2
DB01008Busulfan2Terminated1
DB00531Cyclophosphamide2Completed2
DB00531Cyclophosphamide2Terminated1
DB00091Cyclosporine2Completed1
DB00678Losartan2Active Not Recruiting1
DB00688Mycophenolate mofetil2Completed1
DB06609Odiparcil2Completed1
DB00052Somatotropin2 / 3Terminated1
DB01279Galsulfase4Completed1
DB01279GalsulfaseNot AvailableTerminated1