Mucopolysaccharidosis III
Also known as: Sanfilippo Syndrome (MPS III) / Sanfilippo's syndrome / Sanfilippo Syndrome / Mucopolysaccharidosis Type III / MPS III / MPS3 / Mucopolysaccharidosis Type III (MPS III) / Sanfilippo syndrome (disorder)
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB18483 | Heparan-N-sulfatase (human, recombinant) | 1 / 2 | Terminated | 1 |
| DB16784 | Rebisufligene etisparvovec | 1 / 2 | Terminated | 1 |
| DB00087 | Alemtuzumab | 2 | Completed | 1 |
| DB00631 | Clofarabine | 2 | Completed | 1 |
| DB06189 | Clofarabine | 2 | Completed | 1 |
| DB18483 | Heparan-N-sulfatase (human, recombinant) | 2 | Completed | 1 |
| DB01005 | Hydroxyurea | 2 | Completed | 1 |
| DB01042 | Melphalan | 2 | Completed | 1 |
| DB12722 | N-sulfoglucosamine sulfohydrolase recombinant | 2 | Terminated | 1 |
| DB00026 | Anakinra | 2 / 3 | Completed | 1 |
| DB09061 | Cannabidiol | 2 / 3 | Not Yet Recruiting | 1 |
| DB16784 | Rebisufligene etisparvovec | 2 / 3 | Active Not Recruiting | 1 |