Maple Syrup Urine Disease
Also known as: Maple syrup disease / Maple-syrup-urine disease / Maple syrup urine disease (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB12600 | Phenylbutyric acid | 2 / 3 | Completed | 1 |