Leukodystrophy, Globoid Cell
Also known as: Globoid Cell Leukodystrophy / Krabbe disease / Galactosylceramide beta-galactosidase deficiency (disorder) / Galactosylceramide lipidosis / Krabbe's disease / Globoid cell leukodystrophy, early onset (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB18138 | PBKR03 | 1 / 2 | Suspended | 1 |
DB00087 | Alemtuzumab | 2 | Completed | 1 |
DB00631 | Clofarabine | 2 | Completed | 1 |
DB06189 | Clofarabine | 2 | Completed | 1 |
DB01005 | Hydroxyurea | 2 | Completed | 1 |
DB01042 | Melphalan | 2 | Completed | 1 |
DB01008 | Busulfan | 2 / 3 | Completed | 1 |
DB00531 | Cyclophosphamide | 2 / 3 | Completed | 1 |