Leukodystrophy, Globoid Cell

Also known as: Globoid Cell Leukodystrophy / Krabbe disease / Galactosylceramide beta-galactosidase deficiency (disorder) / Galactosylceramide lipidosis / Krabbe's disease / Globoid cell leukodystrophy, early onset (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB18138PBKR031 / 2Suspended1
DB00087Alemtuzumab2Completed1
DB00631Clofarabine2Completed1
DB06189Clofarabine2Completed1
DB01005Hydroxyurea2Completed1
DB01042Melphalan2Completed1
DB01008Busulfan2 / 3Completed1
DB00531Cyclophosphamide2 / 3Completed1