Sandhoff Disease

Also known as: Sandhoffs Disease / Sandhoff disease (disorder) / GM2 gangliosidosis / GM2 gangliosidosis, unspecified / GM2 gangliosidosis (disorder) / Gangliosidoses, GM2

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB16803Cobnabexagene anvuparvovec1Active Not Recruiting1
DB00650Leucovorin1 / 2Completed1
DB00205Pyrimethamine1 / 2Completed1
DB00087Alemtuzumab2Completed1
DB00631Clofarabine2Completed1
DB06189Clofarabine2Completed1
DB01005Hydroxyurea2Completed1
DB16956L-Acetylleucine2Completed1
DB01042Melphalan2Completed1
DB13201Trenonacog alfa2Completed1
DB01008Busulfan2 / 3Completed1
DB00531Cyclophosphamide2 / 3Completed1
DB00419Miglustat3Completed1
DB14966Venglustat3Active Not Recruiting1
DB00419Miglustat4Terminated1