Gangliosidosis, GM1
Also known as: GM1-Gangliosidosis / GM1 Gangliosidosis / Other gangliosidosis / GM1 gangliosidosis (disorder) / Galactosialidosis / Combined deficiency of sialidase AND beta galactosidase (disorder)
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB18581 | PBGM01 | 1 / 2 | Active Not Recruiting | 1 |
| DB00087 | Alemtuzumab | 2 | Completed | 1 |
| DB00631 | Clofarabine | 2 | Completed | 1 |
| DB06189 | Clofarabine | 2 | Completed | 1 |
| DB01005 | Hydroxyurea | 2 | Completed | 1 |
| DB01042 | Melphalan | 2 | Completed | 1 |
| DB01008 | Busulfan | 2 / 3 | Completed | 1 |
| DB00531 | Cyclophosphamide | 2 / 3 | Completed | 1 |
| DB11735 | Galactose | 3 | Recruiting | 1 |
| DB16948 | Ganglioside GM1 | 3 | Recruiting | 1 |
| DB09153 | Sodium chloride | 3 | Recruiting | 1 |