Cerebrohepatorenal syndrome
Also known as: Zellweger Syndrome / Zellweger syndrome (disorder) / Hyperpipecolic acidaemia / Hyperpipecolic acidemia / Pipecolic acidemia (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB01611 | Hydroxychloroquine | 2 | Completed | 1 |
DB02659 | Cholic Acid | 3 | Completed | 1 |
DB06777 | Chenodeoxycholic acid | Not Available | Terminated | 1 |
DB02659 | Cholic Acid | Not Available | Terminated | 1 |
DB01586 | Ursodeoxycholic acid | Not Available | Terminated | 1 |