Cerebrohepatorenal syndrome

Also known as: Zellweger Syndrome / Zellweger syndrome (disorder) / Hyperpipecolic acidaemia / Hyperpipecolic acidemia / Pipecolic acidemia (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB01611Hydroxychloroquine2Completed1
DB02659Cholic Acid3Completed1
DB06777Chenodeoxycholic acidNot AvailableTerminated1
DB02659Cholic AcidNot AvailableTerminated1
DB01586Ursodeoxycholic acidNot AvailableTerminated1