Tetrahydrobiopterin deficiency

Also known as: Tetrahydrobiopterin Deficiencies / Tetrahydrobiopterin synthesis defect (disorder) / Hyperphenylalaninemia, Non-Phenylketonuric

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00360Sapropterin1Withdrawn1
DB00360Sapropterin2Completed1
DB00360SapropterinNot AvailableCompleted1