Type 1 Mucopolysaccharidosis

Also known as: Mucopolysaccharidosis Type 1 / Mucopolysaccharidosis IS / Mucopolysaccharidosis Type I (MPS I) / Mucopolysaccharidosis I / Mucopolysaccharidosis Type I / Scheie's syndrome / Mucopolysaccharidosis V / Scheie Syndrome / Mucopolysaccharidosis, MPS-I-S (disorder) / Mucopolysaccharidosis, type I / Mucopolysaccharidosis, MPS-I (disorder)

Drug	Drug Name	Drug Description
DB00090	Laronidase	A form of recombinant human alpha-L-iduronidase used to treat Hurler and Hurler-Scheie forms of mucopolysaccharidosis, a genetic deficiency of alpha-L-iduronidase.

Drug	Drug Name	Target	Type
DB00090	Laronidase	Iduronic acid	target

Drug	Drug Name	Phase	Status	Count
DB11105	Benzalkonium	1	Completed	2
DB00030	Insulin human	1	Completed	2
DB00090	Laronidase	1	Terminated	2
DB15336	Valanafusp alfa	1	Completed	2
DB00051	Adalimumab	1 / 2	Active Not Recruiting	1
DB00051	Adalimumab	1 / 2	Completed	1
DB00993	Azathioprine	1 / 2	Completed	1
DB00091	Cyclosporine	1 / 2	Completed	1
DB00090	Laronidase	1 / 2	Completed	1
DB15336	Valanafusp alfa	1 / 2	Completed	2
DB00098	Antithymocyte immunoglobulin (rabbit)	2	Completed	1
DB01008	Busulfan	2	Completed	1
DB00531	Cyclophosphamide	2	Completed	1
DB00090	Laronidase	2	Completed	2
DB00052	Somatotropin	2 / 3	Terminated	1
DB00090	Laronidase	3	Completed	3
DB11105	Benzalkonium	4	Terminated	1
DB00090	Laronidase	4	Completed	3
DB00090	Laronidase	4	Terminated	1
DB16788	Adlinacogene civaparvovec	Not Available	Active Not Recruiting	1
DB11105	Benzalkonium	Not Available	Terminated	1
DB16790	Devafidugene civaparvovec	Not Available	Active Not Recruiting	1
DB00090	Laronidase	Not Available	Completed	1
DB00090	Laronidase	Not Available	Recruiting	1
DB00090	Laronidase	Not Available	Terminated	1
DB16789	Tefidsogene civaparvovec	Not Available	Active Not Recruiting	1