Thalassaemic disorders

Also known as: Thalassaemia / Thalassemia / Thalassemias / Thalassaemia NOS / Thalassaemias

DrugDrug NameDrug Description
DB08826DeferiproneDeferiprone is an oral iron chelator used as a second line agent in thalassemia syndromes when iron overload from blood transfusions occurs. Thalassemias are a type of hereditary anaemia due a defect in the production of hemoglobin. As a result, erythropoiesis, the production of new red blood cells, is impaired. FDA approved on October 14, 2011.
DrugDrug NamePhaseStatusCount
DB01281Abatacept1Recruiting1
DB00087Alemtuzumab1Completed1
DB00098Antithymocyte immunoglobulin (rabbit)1Recruiting1
DB00531Cyclophosphamide1Recruiting1
DB01073Fludarabine1Completed1
DB01005Hydroxyurea1Completed1
DB01042Melphalan1Completed1
DB00688Mycophenolate mofetil1Recruiting1
DB01024Mycophenolic acid1Recruiting1
DB01115Nifedipine1Completed1
DB00552Pentostatin1Recruiting1
DB00877Sirolimus1Recruiting1
DB00864Tacrolimus1Recruiting1
DB04572Thiotepa1Completed1
DB04974AP19031 / 2Active Not Recruiting1
DB01609Deferasirox1 / 2Unknown Status1
DB00746Deferoxamine1 / 2Unknown Status1
DB00087Alemtuzumab2Completed1
DB00087Alemtuzumab2Recruiting1
DB01008Busulfan2Completed1
DB01008Busulfan2Terminated2
DB00493Cefotaxime2Recruiting1
DB00531Cyclophosphamide2Recruiting2
DB00531Cyclophosphamide2Terminated2
DB01262Decitabine2Completed1
DB00746Deferoxamine2Completed1
DB01073Fludarabine2Completed1
DB01073Fludarabine2Recruiting1
DB01073Fludarabine2Terminated2
DB01005Hydroxyurea2Recruiting1
DB00130L-Glutamine2Completed3
DB12281Luspatercept2Recruiting1
DB12583Maltodextrin2Completed1
DB00008Peginterferon alfa-2a2Completed1
DB00552Pentostatin2Recruiting1
DB00252Phenytoin2Terminated1
DB00635Prednisone2Terminated1
DB00811Ribavirin2Completed1
DB00877Sirolimus2Recruiting1
DB00864Tacrolimus2Terminated1
DB01041Thalidomide2Recruiting2
DB00087Alemtuzumab2 / 3Active Not Recruiting1
DB00381Amlodipine2 / 3Completed1
DB01008Busulfan2 / 3Active Not Recruiting1
DB00531Cyclophosphamide2 / 3Active Not Recruiting1
DB01073Fludarabine2 / 3Active Not Recruiting1
DB00203Sildenafil2 / 3Completed1
DB00381Amlodipine3Completed1
DB01609Deferasirox3Completed1
DB01609Deferasirox4Completed2
DB00746Deferoxamine4Completed1
DB00125L-Arginine4Recruiting1
DB00203Sildenafil4Recruiting1
DB08934Sofosbuvir4Completed1
DB02772Sucrose4Completed1
DB11613Velpatasvir4Completed1
DB00399Zoledronic acid4Completed1
DB00819AcetazolamideNot AvailableRecruiting1
DB06151AcetylcysteineNot AvailableCompleted1
DB00092AlefaceptNot AvailableTerminated1
DB00087AlemtuzumabNot AvailableTerminated1
DB01008BusulfanNot AvailableTerminated1
DB09110Coenzyme MNot AvailableTerminated1
DB00531CyclophosphamideNot AvailableTerminated1
DB01262DecitabineNot AvailableCompleted1
DB01609DeferasiroxNot AvailableCompleted2
DB08826DeferiproneNot AvailableCompleted2
DB00746DeferoxamineNot AvailableCompleted2
DB01073FludarabineNot AvailableTerminated1
DB01005HydroxyureaNot AvailableRecruiting1
DB00125L-ArginineNot AvailableCompleted1
DB00203SildenafilNot AvailableCompleted1
DB00163Vitamin ENot AvailableCompleted1