Thalassaemic disorders

Also known as: Thalassemia / Thalassemias / Thalassaemia / Thalassaemias / Thalassemia, unspecified / Thalassemia syndrome (disorder) / Thalassaemia NOS / Thalassemia (disorder)

DrugDrug NameDrug Description
DB08826DeferiproneAn iron chelator used to treat patients with transfusional iron overload caused by thalassemia syndromes.
DrugDrug NamePhaseStatusCount
DB00087Alemtuzumab1Completed1
DB00098Antithymocyte immunoglobulin (rabbit)1Active Not Recruiting1
DB00531Cyclophosphamide1Active Not Recruiting1
DB01073Fludarabine1Completed1
DB01005Hydroxyurea1Completed1
DB01592Iron1Completed1
DB01042Melphalan1Completed1
DB00688Mycophenolate mofetil1Active Not Recruiting1
DB01024Mycophenolic acid1Active Not Recruiting1
DB01115Nifedipine1Completed1
DB00552Pentostatin1Active Not Recruiting1
DB18608Sapablursen1Completed1
DB00877Sirolimus1Active Not Recruiting1
DB00864Tacrolimus1Active Not Recruiting1
DB04572Thiotepa1Completed1
DB01609Deferasirox1 / 2Unknown Status1
DB00746Deferoxamine1 / 2Unknown Status1
DB04974Rimiducid1 / 2Terminated2
DB04572Thiotepa1 / 2Completed1
DB00087Alemtuzumab2Completed1
DB00087Alemtuzumab2Recruiting1
DB00087Alemtuzumab2Terminated2
DB00098Antithymocyte immunoglobulin (rabbit)2Recruiting1
DB00188Bortezomib2Recruiting1
DB01008Busulfan2Completed1
DB01008Busulfan2Terminated2
DB00531Cyclophosphamide2Active Not Recruiting1
DB00531Cyclophosphamide2Recruiting2
DB00531Cyclophosphamide2Terminated2
DB01262Decitabine2Completed1
DB01609Deferasirox2Completed1
DB00746Deferoxamine2Completed2
DB01234Dexamethasone2Recruiting1
DB18176Etavopivat2Recruiting1
DB00099Filgrastim2Terminated1
DB01073Fludarabine2Active Not Recruiting1
DB01073Fludarabine2Completed1
DB01073Fludarabine2Recruiting1
DB01073Fludarabine2Terminated2
DB15726Human Umbilical Cord Mesenchymal Stem Cells2Completed1
DB01005Hydroxyurea2Terminated1
DB00130L-Glutamine2Completed2
DB00130L-Glutamine2Terminated1
DB12281Luspatercept2Completed1
DB12583Maltodextrin2Completed1
DB16236Mitapivat2Active Not Recruiting1
DB00688Mycophenolate mofetil2Recruiting1
DB00008Peginterferon alfa-2a2Completed1
DB00552Pentostatin2Recruiting1
DB00252Phenytoin2Terminated1
DB00635Prednisone2Terminated1
DB00811Ribavirin2Completed1
DB00073Rituximab2Recruiting1
DB00936Salicylic acid2Terminated1
DB00877Sirolimus2Recruiting1
DB00864Tacrolimus2Recruiting1
DB00864Tacrolimus2Terminated2
DB01041Thalidomide2Unknown Status2
DB00087Alemtuzumab2 / 3Completed1
DB00381Amlodipine2 / 3Completed1
DB00098Antithymocyte immunoglobulin (rabbit)2 / 3Completed1
DB01008Busulfan2 / 3Completed1
DB01373Calcium2 / 3Completed1
DB00531Cyclophosphamide2 / 3Completed1
DB00746Deferoxamine2 / 3Completed1
DB15572Exagamglogene autotemcel2 / 3Active Not Recruiting1
DB00099Filgrastim2 / 3Completed1
DB01073Fludarabine2 / 3Completed1
DB01005Hydroxyurea2 / 3Completed1
DB00203Sildenafil2 / 3Completed1
DB01041Thalidomide2 / 3Completed1
DB00381Amlodipine3Completed1
DB01609Deferasirox3Completed1
DB15572Exagamglogene autotemcel3Enrolling by Invitation1
DB15572Exagamglogene autotemcel3Recruiting2
DB00125Arginine4Recruiting1
DB01609Deferasirox4Completed1
DB11242Gelatin4Unknown Status2
DB06603Panobinostat4Recruiting1
DB00008Peginterferon alfa-2a4Completed1
DB00811Ribavirin4Completed1
DB08877Ruxolitinib4Recruiting1
DB00203Sildenafil4Recruiting1
DB08934Sofosbuvir4Completed1
DB10319Streptococcus pneumoniae type 1 capsular polysaccharide antigen4Completed1
DB10329Streptococcus pneumoniae type 10a capsular polysaccharide antigen4Completed1
DB10330Streptococcus pneumoniae type 11a capsular polysaccharide antigen4Completed1
DB10331Streptococcus pneumoniae type 12f capsular polysaccharide antigen4Completed1
DB10332Streptococcus pneumoniae type 14 capsular polysaccharide antigen4Completed1
DB10333Streptococcus pneumoniae type 15b capsular polysaccharide antigen4Completed1
DB10334Streptococcus pneumoniae type 17f capsular polysaccharide antigen4Completed1
DB10335Streptococcus pneumoniae type 18c capsular polysaccharide antigen4Completed1
DB10337Streptococcus pneumoniae type 19a capsular polysaccharide antigen4Completed1
DB10336Streptococcus pneumoniae type 19f capsular polysaccharide antigen4Completed1
DB10320Streptococcus pneumoniae type 2 capsular polysaccharide antigen4Completed1
DB10338Streptococcus pneumoniae type 20 capsular polysaccharide antigen4Completed1
DB10339Streptococcus pneumoniae type 22f capsular polysaccharide antigen4Completed1
DB10340Streptococcus pneumoniae type 23f capsular polysaccharide antigen4Completed1
DB10321Streptococcus pneumoniae type 3 capsular polysaccharide antigen4Completed1
DB10341Streptococcus pneumoniae type 33f capsular polysaccharide antigen4Completed1
DB10322Streptococcus pneumoniae type 4 capsular polysaccharide antigen4Completed1
DB10323Streptococcus pneumoniae type 5 capsular polysaccharide antigen4Completed1
DB10296Streptococcus pneumoniae type 6A capsular polysaccharide diphtheria CRM197 protein conjugate antigen4Completed1
DB10324Streptococcus pneumoniae type 6b capsular polysaccharide antigen4Completed1
DB10325Streptococcus pneumoniae type 7f capsular polysaccharide antigen4Completed1
DB10326Streptococcus pneumoniae type 8 capsular polysaccharide antigen4Completed1
DB10327Streptococcus pneumoniae type 9n capsular polysaccharide antigen4Completed1
DB10328Streptococcus pneumoniae type 9v capsular polysaccharide antigen4Completed1
DB02772Sucrose4Completed2
DB11613Velpatasvir4Completed1
DB09322Zinc sulfate4Completed1
DB00399Zoledronic acid4Completed1
DB00819AcetazolamideNot AvailableCompleted1
DB06151AcetylcysteineNot AvailableCompleted1
DB00092AlefaceptNot AvailableTerminated1
DB00087AlemtuzumabNot AvailableTerminated1
DB00125ArginineNot AvailableCompleted1
DB01008BusulfanNot AvailableTerminated1
DB00631ClofarabineNot AvailableCompleted1
DB09110Coenzyme MNot AvailableTerminated1
DB00531CyclophosphamideNot AvailableTerminated1
DB01262DecitabineNot AvailableCompleted1
DB01609DeferasiroxNot AvailableCompleted2
DB08826DeferiproneNot AvailableCompleted2
DB00746DeferoxamineNot AvailableCompleted2
DB01073FludarabineNot AvailableCompleted2
DB01073FludarabineNot AvailableTerminated1
DB01005HydroxyureaNot AvailableCompleted1
DB16956L-AcetylleucineNot AvailableCompleted1
DB01042MelphalanNot AvailableCompleted1
DB00203SildenafilNot AvailableCompleted1
DB04572ThiotepaNot AvailableCompleted1
DB00163Vitamin ENot AvailableCompleted1