Glycogen Storage Disease
Also known as: Glycogen Storage Disorders / Glycogen storage disorder / Glycogen storage disease, unspecified / Glycogenosis / Glycogenoses / Glycogen storage disease (disorder) / Glycogen storage disorder NOS
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB18554 | mRNA-3745 | 1 / 2 | Recruiting | 1 |
DB01272 | Alglucosidase alfa | Not Available | Completed | 1 |
DB11677 | Triheptanoin | Not Available | No Longer Available | 1 |