Fabry's Disease

Also known as: Fabry / Fabry´s Disease / Fabry Disease / Fabry (-Anderson) disease / Angiokeratoma corporis diffusum universale / Deficiency of alpha-galactosidase (disorder) / Alpha galactosidase A deficiency / Fabry's disease (disorder)

DrugDrug NameDrug Description
DB15874Agalsidase alfaA recombinant human alpha-galactosidase indicated to treat Fabry disease, a genetic deficiency in the enzyme leading to buildup of globotriaosylceramide.
DB00103Agalsidase betaA recombinant human alpha-galactosidase indicated to treat Fabry disease, a genetic deficiency in the enzyme leading to buildup of globotriaosylceramide.
DB05018MigalastatAn alpha-galactosidase A chaperone used for the treatment of Fabry disease in patients with an amenable galactosidase alpha gene (GLA) variant.
DB14992Pegunigalsidase alfaA recombinant form of human α-galactosidase-A indicated for long-term enzyme replacement therapy in patients with Fabry disease.
DrugDrug NamePhaseStatusCount
DB15874Agalsidase alfa1Completed3
DB00103Agalsidase beta1Active Not Recruiting1
DB00103Agalsidase beta1Completed1
DB11105Benzalkonium1Active Not Recruiting1
DB01362Iohexol1Terminated1
DB14872Lucerastat1Completed1
DB05018Migalastat1Completed3
DB09153Sodium chloride1Completed1
DB183234D-3101 / 2Active Not Recruiting2
DB17651AVR-RD-011 / 2Terminated1
DB12000Apabetalone1 / 2Withdrawn1
DB11105Benzalkonium1 / 2Completed1
DB16808Isaralgagene civaparvovec1 / 2Active Not Recruiting1
DB14992Pegunigalsidase alfa1 / 2Completed3
DB17654AL-012112Recruiting1
DB15874Agalsidase alfa2Completed8
DB00103Agalsidase beta2Completed3
DB00103Agalsidase beta2Terminated1
DB06292Dapagliflozin2Not Yet Recruiting1
DB00996Gabapentin2Withdrawn1
DB05018Migalastat2Completed5
DB05018Migalastat2Terminated1
DB11105Benzalkonium2 / 3Recruiting1
DB14992Pegunigalsidase alfa2 / 3Recruiting1
DB15874Agalsidase alfa3Completed5
DB15874Agalsidase alfa3Recruiting2
DB15874Agalsidase alfa3Terminated1
DB00103Agalsidase beta3Completed4
DB00103Agalsidase beta3Recruiting3
DB11105Benzalkonium3Completed3
DB11105Benzalkonium3Withdrawn1
DB14872Lucerastat3Active Not Recruiting1
DB14872Lucerastat3Completed1
DB05018Migalastat3Active Not Recruiting1
DB05018Migalastat3Completed4
DB05018Migalastat3Recruiting2
DB05018Migalastat3Terminated1
DB14992Pegunigalsidase alfa3Active Not Recruiting2
DB14992Pegunigalsidase alfa3Completed3
DB14992Pegunigalsidase alfa3Withdrawn1
DB14966Venglustat3Recruiting2
DB00316Acetaminophen4Recruiting1
DB15874Agalsidase alfa4Active Not Recruiting1
DB15874Agalsidase alfa4Completed2
DB15874Agalsidase alfa4Unknown Status1
DB15874Agalsidase alfa4Withdrawn1
DB00103Agalsidase beta4Completed6
DB00103Agalsidase beta4Recruiting2
DB00103Agalsidase beta4Withdrawn2
DB01234Dexamethasone4Recruiting1
DB01075Diphenhydramine4Recruiting1
DB00471Montelukast4Recruiting1
DB15874Agalsidase alfaNot AvailableCompleted2
DB15874Agalsidase alfaNot AvailableNo Longer Available1
DB00103Agalsidase betaNot AvailableCompleted4
DB00103Agalsidase betaNot AvailableRecruiting1
DB11842Angiotensin IINot AvailableCompleted1
DB00584EnalaprilNot AvailableCompleted1
DB16808Isaralgagene civaparvovecNot AvailableEnrolling by Invitation1
DB00678LosartanNot AvailableCompleted1
DB05018MigalastatNot AvailableActive Not Recruiting1
DB05018MigalastatNot AvailableApproved for Marketing1
DB05018MigalastatNot AvailableRecruiting1
DB00910ParicalcitolNot AvailableCompleted1
DB14992Pegunigalsidase alfaNot AvailableAvailable1
DB14992Pegunigalsidase alfaNot AvailableRecruiting1
DB00809TropicamideNot AvailableCompleted1