Fabry's Disease

Also known as: Fabry's disease / Fabry Disease / Angiokeratoma corporis diffusum universale / Fabry (-Anderson) disease / Lipidoses / Alpha galactosidase A deficiency

DrugDrug NameDrug Description
DB00103Agalsidase betaA form of recombinant human alpha-galactosidase A enzyme used to treat Fabry disease, a genetic deficiency in the enzyme leading to buildup of globotriaosylceramide.
DB05018MigalastatAn alpha-galactosidase A chaperone used for the treatment of Fabry disease in patients with an amenable galactosidase alpha gene (GLA) variant.
DrugDrug NamePhaseStatusCount
DB00103Agalsidase beta1Completed3
DB14872Lucerastat1Completed1
DB05018Migalastat1Completed3
DB09153Sodium chloride1Completed1
DB12000Apabetalone1 / 2Not Yet Recruiting1
DB14992Pegunigalsidase alfa1 / 2Active Not Recruiting1
DB14992Pegunigalsidase alfa1 / 2Completed2
DB00103Agalsidase beta2Completed9
DB00103Agalsidase beta2Terminated1
DB00996Gabapentin2Withdrawn1
DB05018Migalastat2Completed5
DB05018Migalastat2Terminated1
DB00103Agalsidase beta3Active Not Recruiting1
DB00103Agalsidase beta3Completed6
DB14872Lucerastat3Recruiting2
DB05018Migalastat3Active Not Recruiting2
DB05018Migalastat3Completed2
DB05018Migalastat3Not Yet Recruiting1
DB05018Migalastat3Recruiting1
DB05018Migalastat3Terminated1
DB14992Pegunigalsidase alfa3Active Not Recruiting3
DB14992Pegunigalsidase alfa3Enrolling by Invitation2
DB14992Pegunigalsidase alfa3Withdrawn1
DB00103Agalsidase beta4Completed7
DB00103Agalsidase beta4Recruiting2
DB00103Agalsidase beta4Unknown Status1
DB00103Agalsidase beta4Withdrawn1
DB00103Agalsidase betaNot AvailableCompleted2
DB00103Agalsidase betaNot AvailableNo Longer Available1
DB00103Agalsidase betaNot AvailableNot Yet Recruiting1
DB11842Angiotensin IINot AvailableCompleted1
DB00584EnalaprilNot AvailableCompleted1
DB01362IohexolNot AvailableTerminated1
DB00678LosartanNot AvailableCompleted1
DB05018MigalastatNot AvailableApproved for Marketing1
DB05018MigalastatNot AvailableRecruiting2
DB00910ParicalcitolNot AvailableCompleted1
DB00809TropicamideNot AvailableCompleted1