Hurler's Syndrome

Also known as: Hurler Syndrome / Dysostosis multiplex / MPS I H / Hurler's disease / Mucopolysaccharidosis I

DrugDrug NameDrug Description
DB00090LaronidaseA form of recombinant human alpha-L-iduronidase used to treat Hurler and Hurler-Scheie forms of mucopolysaccharidosis, a genetic deficiency of alpha-L-iduronidase.
DrugDrug NameTargetType
DB00090LaronidaseIduronic acidtarget
DrugDrug NamePhaseStatusCount
DB01281Abatacept1Completed1
DB00090Laronidase1Completed2
DB04572Thiotepa1 / 2Recruiting1
DB00087Alemtuzumab2Completed1
DB00087Alemtuzumab2Terminated1
DB01008Busulfan2Completed1
DB01008Busulfan2Terminated1
DB00531Cyclophosphamide2Completed1
DB00531Cyclophosphamide2Terminated1
DB00091Cyclosporine2Completed1
DB00090Laronidase2Completed2
DB00688Mycophenolate mofetil2Completed1
DB00090Laronidase3Completed2
DB00090Laronidase4Completed2
DB00090Laronidase4Recruiting1
DB00090LaronidaseNot AvailableTerminated1
DB04974RimiducidNot AvailableNo Longer Available1
DB00052SomatotropinNot AvailableWithdrawn1