Hurler-Scheie Syndrome
Also known as: Mucopolysaccharidosis, MPS-I-H/S (disorder) / Mucopolysaccharidosis IH/S / Mucopolysaccharidosis, type I / Mucopolysaccharidosis I / Mucopolysaccharidosis, MPS-I (disorder)
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB00090 | Laronidase | A form of recombinant human alpha-L-iduronidase used to treat Hurler and Hurler-Scheie forms of mucopolysaccharidosis, a genetic deficiency of alpha-L-iduronidase. |
| Drug | Drug Name | Target | Type |
|---|---|---|---|
| DB00090 | Laronidase | Iduronic acid | target |
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB00090 | Laronidase | 1 | Terminated | 1 |
| DB00090 | Laronidase | 2 | Completed | 1 |
| DB00090 | Laronidase | 3 | Completed | 3 |
| DB11105 | Benzalkonium | 4 | Terminated | 1 |
| DB00090 | Laronidase | 4 | Completed | 2 |
| DB00090 | Laronidase | 4 | Terminated | 1 |
| DB00090 | Laronidase | Not Available | Completed | 1 |