Lysosomal Storage Diseases
Also known as: Lysosomal Disease / Lysosomal Storage Disorders / Lysosomal Diseases / Lysosomal Storage Disease / Lysosomal Storage Disorder / Disorder of lysosomal enzyme (disorder)
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB00087 | Alemtuzumab | 1 | Completed | 1 |
| DB01073 | Fludarabine | 1 | Completed | 1 |
| DB01005 | Hydroxyurea | 1 | Completed | 1 |
| DB00090 | Laronidase | 1 | Terminated | 2 |
| DB01042 | Melphalan | 1 | Completed | 1 |
| DB04572 | Thiotepa | 1 | Completed | 1 |
| DB16804 | Bomtabegagene bavoparvovec | 1 / 2 | Recruiting | 1 |
| DB00959 | Methylprednisolone | 1 / 2 | Recruiting | 1 |
| DB00635 | Prednisone | 1 / 2 | Recruiting | 1 |
| DB00073 | Rituximab | 1 / 2 | Recruiting | 1 |
| DB00877 | Sirolimus | 1 / 2 | Recruiting | 1 |
| DB00087 | Alemtuzumab | Not Available | Completed | 1 |
| DB00631 | Clofarabine | Not Available | Completed | 1 |
| DB06189 | Clofarabine | Not Available | Completed | 1 |
| DB00091 | Cyclosporine | Not Available | Completed | 1 |
| DB00090 | Laronidase | Not Available | Completed | 1 |
| DB01042 | Melphalan | Not Available | Completed | 1 |
| DB00688 | Mycophenolate mofetil | Not Available | Completed | 1 |
| DB04974 | Rimiducid | Not Available | No Longer Available | 1 |