Hyperphenylalaninemia, Non-Phenylketonuric

Also known as: Non-Phenylketonuric Hyperphenylalaninemia / Tetrahydrobiopterin synthesis defect (disorder) / Tetrahydrobiopterin deficiency

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00360Sapropterin2Completed1