Phenylalanine Hydroxylase Deficiencies
Also known as: Phenylalanine Hydroxylase Deficiency / Classical phenylketonuria / Classical phenylketonuria (disorder) / Phenylketonuria I / Phenylpyruvic oligophrenia / Phenylketonuria (PKU) / Phenylketonuria / Phenylketonurias / Phenylalaninaemia / Phenylalaninemia / PKU
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB00360 | Sapropterin | 2 / 3 | Terminated | 1 |