Phenylalanine Hydroxylase Deficiencies

Also known as: Phenylalanine Hydroxylase Deficiency / Classical phenylketonuria / Classical phenylketonuria (disorder) / Phenylketonuria I / Phenylpyruvic oligophrenia / Phenylketonuria (PKU) / Phenylketonuria / Phenylketonurias / Phenylalaninaemia / Phenylalaninemia / PKU

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00360Sapropterin2 / 3Terminated1