Spinal Muscular Atrophy Type II

Also known as: Muscular Atrophy, Spinal, Type II / Spinal muscular atrophy, type II (disorder) / Spinal muscular atrophy, unspecified / Muscular Atrophy, Spinal / Spinal amyotrophy / Spinal muscular atrophy (disorder) / Spinal muscular atrophy

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB06819Phenylbutyric acid1 / 2Terminated1
DB05185Olesoxime2Completed1
DB16096Apitegromab3Active Not Recruiting1
DB02325Isopropyl alcohol3Active Not Recruiting1
DB15528Onasemnogene abeparvovec3Active Not Recruiting1
DB13161NusinersenNot AvailableRecruiting1