Spinal Muscular Atrophy Type I

Also known as: Spinal muscular atrophy NOS / Muscular Atrophy, Spinal / Spinal muscular atrophy, unspecified / Spinal amyotrophy / Spinal muscular atrophy

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00583Levocarnitine1 / 2Completed1
DB06819Phenylbutyric acid1 / 2Terminated1
DB00313Valproic acid1 / 2Completed1
DB15528Onasemnogene abeparvovec3Recruiting1
DB15528Onasemnogene abeparvovec4Recruiting1