Niemann-Pick Type C Disease
Also known as: Niemann-Pick Disease Type C / Niemann-Pick Disease, Type C / Niemann-Pick disease, type C (disorder)
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB15146 | Adrabetadex | 1 / 2 | Recruiting | 1 |
| DB00151 | Cysteine | 1 / 2 | Completed | 1 |
| DB15379 | Hydroxypropyl betadex | 1 / 2 | Recruiting | 1 |
| DB18502 | AZ-3102 | 2 | Active Not Recruiting | 1 |
| DB15146 | Adrabetadex | 2 | Withdrawn | 1 |
| DB00087 | Alemtuzumab | 2 | Terminated | 1 |
| DB01008 | Busulfan | 2 | Terminated | 1 |
| DB00531 | Cyclophosphamide | 2 | Terminated | 1 |
| DB16956 | L-Acetylleucine | 2 | Completed | 1 |
| DB00419 | Miglustat | 2 | Completed | 1 |
| DB13201 | Trenonacog alfa | 2 | Completed | 1 |
| DB15146 | Adrabetadex | 2 / 3 | Completed | 1 |
| DB15146 | Adrabetadex | 2 / 3 | Terminated | 2 |
| DB05025 | Arimoclomol | 2 / 3 | Active Not Recruiting | 1 |
| DB15146 | Adrabetadex | 3 | Terminated | 1 |
| DB16956 | L-Acetylleucine | 3 | Active Not Recruiting | 1 |
| DB00419 | Miglustat | 3 | Completed | 1 |
| DB13201 | Trenonacog alfa | 3 | Active Not Recruiting | 1 |
| DB00419 | Miglustat | 4 | Completed | 1 |
| DB05025 | Arimoclomol | Not Available | Available | 1 |