LGMD2B
Also known as: Miyoshi Myopathy / Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB11921 | Deflazacort | 2 / 3 | Completed | 1 |