Hunter Syndrome

Also known as: Mucopolysaccharidosis Type II / Hunter's syndrome / Mucopolysaccharidosis II (MPS II) / Hunter Syndrome (MPS II) / Mucopolysaccharidosis II / Mucopolysaccharidosis Type II (MPS II) / MPS II / Mucopolysaccharidosis, type II / Mucopolysaccharidosis, MPS-II (disorder)

DrugDrug NameDrug Description
DB01271IdursulfaseA purified lysosomal enzyme used as a replacement therapy for Hunter syndrome in pediatric and adult patients.
DrugDrug NamePhaseStatusCount
DB17630AGT-1821Completed1
DB01272Alglucosidase alfa1Recruiting1
DB09051Elosulfase alfa1Recruiting1
DB01279Galsulfase1Recruiting1
DB18520HMI-2031Withdrawn1
DB01271Idursulfase1Recruiting1
DB00090Laronidase1Recruiting1
DB11563Sebelipase alfa1Recruiting1
DB12366Vestronidase alfa1Recruiting1
DB00051Adalimumab1 / 2Active Not Recruiting1
DB00051Adalimumab1 / 2Completed1
DB01271Idursulfase1 / 2Active Not Recruiting1
DB01271Idursulfase1 / 2Completed1
DB15633Pabinafusp alfa1 / 2Completed1
DB16789Tefidsogene civaparvovec1 / 2Terminated1
DB17628Tividenofusp alfa1 / 2Recruiting1
DB00087Alemtuzumab2Completed1
DB01008Busulfan2Completed1
DB00531Cyclophosphamide2Completed1
DB00091Cyclosporine2Completed1
DB01271Idursulfase2Unknown Status1
DB16190Idursulfase beta2Unknown Status1
DB00688Mycophenolate mofetil2Completed1
DB15633Pabinafusp alfa2Active Not Recruiting1
DB15633Pabinafusp alfa2Completed1
DB01271Idursulfase2 / 3Active Not Recruiting1
DB01271Idursulfase2 / 3Completed3
DB01271Idursulfase2 / 3Not Yet Recruiting1
DB01271Idursulfase2 / 3Recruiting1
DB15633Pabinafusp alfa2 / 3Active Not Recruiting1
DB15633Pabinafusp alfa2 / 3Completed1
DB00052Somatotropin2 / 3Terminated1
DB17628Tividenofusp alfa2 / 3Enrolling by Invitation1
DB17628Tividenofusp alfa2 / 3Recruiting1
DB01271Idursulfase3Recruiting1
DB16190Idursulfase beta3Completed1
DB15633Pabinafusp alfa3Enrolling by Invitation1
DB15633Pabinafusp alfa3Recruiting1
DB00028Human immunoglobulin G4Recruiting1
DB01271Idursulfase4Active Not Recruiting1
DB01271Idursulfase4Completed1
DB01271Idursulfase4Recruiting2
DB00563Methotrexate4Recruiting1
DB00073Rituximab4Recruiting1
DB16788Adlinacogene civaparvovecNot AvailableActive Not Recruiting1
DB16790Devafidugene civaparvovecNot AvailableActive Not Recruiting1
DB01271IdursulfaseNot AvailableAvailable1
DB01271IdursulfaseNot AvailableCompleted2
DB16789Tefidsogene civaparvovecNot AvailableActive Not Recruiting1