Mucopolysaccharidosis II (MPS II)
Also known as: Mucopolysaccharidosis Type II / Hunter Syndrome / Hunter's syndrome / Hunter Syndrome (MPS II) / Mucopolysaccharidosis II / Mucopolysaccharidosis Type II (MPS II) / MPS II / Mucopolysaccharidosis, type II / Mucopolysaccharidosis, MPS-II (disorder)
Drug | Drug Name | Drug Description |
---|---|---|
DB01271 | Idursulfase | A purified lysosomal enzyme used as a replacement therapy for Hunter syndrome in pediatric and adult patients. |
Drug | Drug Name | Target | Type |
---|---|---|---|
DB01271 | Idursulfase | Perilipin-3 | target |
DB01271 | Idursulfase | Dermatan sulfate | target |
DB01271 | Idursulfase | Heparan sulfate | target |