Sly Syndrome Completed Phase 3 Trials for Vestronidase alfa (DB12366)

IndicationStatusPhase
DBCOND0040268 (Sly Syndrome)Completed3
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT02432144A Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Therapy in Subjects With Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7)Treatment
NCT02230566A Phase 3 Study of UX003 Recombinant Human Betaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7)Treatment