Sphingolipidoses

Also known as: Sphingolipidosis / Sphingolipidosis, unspecified / Sphingolipidosis (disorder) / Niemann-Pick disease / Niemann-Pick disease, unspecified / Sphingomyelin/cholesterol lipidosis (disorder) / Sphingomyelin lipidosis / Niemann-Pick Diseases

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00087Alemtuzumab2Completed1
DB00087Alemtuzumab2Terminated1
DB01008Busulfan2Completed1
DB01008Busulfan2Terminated1
DB00531Cyclophosphamide2Completed1
DB00531Cyclophosphamide2Terminated1
DB00091Cyclosporine2Completed1
DB00688Mycophenolate mofetil2Completed1