Wolman's Disease Completed Phase 2 / 3 Trials for Busulfan (DB01008)

Also known as: Wolman Disease / Disease, Wolman / Lipidoses NOS / Cerebrotendinous cholesterosis [van Bogaert-Scherer-Epstein]

IndicationStatusPhase
DBCOND0040271 (Wolman's Disease)Completed2 / 3
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT00176904Stem Cell Transplant for Inborn Errors of MetabolismTreatment