Wolman's Disease Terminated Phase 2 Trials for Busulfan (DB01008)

Also known as: Wolman Disease / Disease, Wolman / Lipidoses NOS / Cerebrotendinous cholesterosis [van Bogaert-Scherer-Epstein]

IndicationStatusPhase
DBCOND0040271 (Wolman's Disease)Terminated2
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT00668564Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of MetabolismTreatment