Hutchinson-Gilford Progeria Syndrome

Also known as: Progeria / Other specified endocrine disorders / Hutchinson-Gilford syndrome (disorder)

DrugDrug NameDrug Description
DB06448LonafarnibA potent farnesyl transferase inhibitor used to reduce mortality associated with Hutchinson-Gilford progeria syndrome (HGPS) and other progeroid laminopathies.
DrugDrug NamePhaseStatusCount
DB17634Progerinin1Completed1
DB01590Everolimus1 / 2Enrolling by Invitation1
DB06448Lonafarnib1 / 2Enrolling by Invitation1
DB00877Sirolimus1 / 2Completed1
DB06448Lonafarnib2Active Not Recruiting1
DB06448Lonafarnib2Completed2
DB00175Pravastatin2Active Not Recruiting1
DB00175Pravastatin2Completed2
DB00399Zoledronic acid2Active Not Recruiting1
DB00399Zoledronic acid2Completed2
DB06448LonafarnibNot AvailableApproved for Marketing1