Severe Osteopetrosis

Also known as: Infantile malignant osteopetrosis (disorder) / Osteopetrosis / Osteopetrosis (disorder) / Marble bone disease / Albers-Schonberg disease

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00087Alemtuzumab2 / 3Completed1
DB01008Busulfan2 / 3Completed1
DB00531Cyclophosphamide2 / 3Completed1
DB01073Fludarabine2 / 3Completed1