SMA

Also known as: Spinal Muscular Atrophies / SMA - Spinal Muscular Atrophy / Spinal Muscular Atrophy (SMA) / Muscular Atrophy, Spinal / Spinal Muscular Atrophy / SMAS / Spinal muscular atrophy, unspecified / Spinal amyotrophy / Spinal muscular atrophy (disorder) / Structure of superficial musculoaponeurotic system (body structure) / Superficial Musculoaponeurotic System

DrugDrug NameDrug Description
DB13161NusinersenA medication used to treat spinal muscular atrophy.
DB15528Onasemnogene abeparvovecA gene therapy used to treat neonatal and infant patients with spinal muscular atrophy caused by bi-allelic mutations in the survival motor neuron 1 (SMN1) gene.
DB15305RisdiplamAn oral mRNA splicing modifier used in the treatment of spinal muscular atrophy (SMA).
DrugDrug NamePhaseStatusCount
DB13161Nusinersen0Withdrawn1
DB18418BIIB1151Recruiting1
DB02325Isopropyl alcohol1Terminated1
DB01167Itraconazole1Completed1
DB00683Midazolam1Completed1
DB13161Nusinersen1Completed3
DB00338Omeprazole1Completed1
DB15528Onasemnogene abeparvovec1Terminated1
DB15305Risdiplam1Completed4
DB00313Valproic acid1Completed1
DB14918Branaplam1 / 2Completed1
DB01005Hydroxyurea1 / 2Completed2
DB13161Nusinersen1 / 2Completed1
DB06819Phenylbutyric acid1 / 2Completed1
DB11640Amifampridine2Completed1
DB16096Apitegromab2Active Not Recruiting1
DB00482Celecoxib2Terminated1
DB00007Leuprolide2Completed1
DB00583Levocarnitine2Completed2
DB18466NMD-6702Recruiting1
DB13161Nusinersen2Active Not Recruiting1
DB13161Nusinersen2Completed1
DB13161Nusinersen2Terminated1
DB05185Olesoxime2Completed1
DB00545Pyridostigmine2Completed1
DB15256Reldesemtiv2Completed1
DB15305Risdiplam2Active Not Recruiting2
DB15305Risdiplam2Completed2
DB15305Risdiplam2Not Yet Recruiting1
DB00052Somatotropin2Completed1
DB00624Testosterone2Completed1
DB00313Valproic acid2Completed2
DB06637Dalfampridine2 / 3Completed1
DB01005Hydroxyurea2 / 3Completed1
DB00740Riluzole2 / 3Completed1
DB15305Risdiplam2 / 3Recruiting1
DB16096Apitegromab3Active Not Recruiting2
DB02325Isopropyl alcohol3Active Not Recruiting1
DB02325Isopropyl alcohol3Completed3
DB02325Isopropyl alcohol3Recruiting1
DB00583Levocarnitine3Unknown Status1
DB13161Nusinersen3Active Not Recruiting1
DB13161Nusinersen3Completed2
DB13161Nusinersen3Enrolling by Invitation1
DB13161Nusinersen3Recruiting1
DB13161Nusinersen3Terminated1
DB15528Onasemnogene abeparvovec3Active Not Recruiting1
DB15528Onasemnogene abeparvovec3Completed3
DB15528Onasemnogene abeparvovec3Recruiting1
DB16337Talditercept alfa3Active Not Recruiting1
DB00313Valproic acid3Unknown Status1
DB10791Influenza A virus A/California/7/2009 X-179A (H1N1) antigen (formaldehyde inactivated)4Completed1
DB14445Influenza A virus A/Victoria/210/2009 X-187 (H3N2) antigen (formaldehyde inactivated)4Completed1
DB10794Influenza B virus B/Brisbane/60/2008 antigen (formaldehyde inactivated)4Completed1
DB13161Nusinersen4Active Not Recruiting1
DB15305Risdiplam4Active Not Recruiting1
DB15305Risdiplam4Not Yet Recruiting1
DB15305Risdiplam4Recruiting2
DB02325Isopropyl alcoholNot AvailableRecruiting1
DB13161NusinersenNot AvailableCompleted4
DB13161NusinersenNot AvailableRecruiting5
DB15528Onasemnogene abeparvovecNot AvailableRecruiting1
DB15305RisdiplamNot AvailableApproved for Marketing1
DB15305RisdiplamNot AvailableRecruiting1