Non-transfusion Dependent Thalassemia

Also known as: Non-transfusion-dependent thalassemia / Non-Transfusion-Dependent Thalassemia Syndromes / Non-transfusion dependent thalassaemia / Thalassemia / (Thalassaemia (& Mediterranean anaemia)) or (leptocytosis, hereditary) / (Thalassaemia) or (pyruvate kinase deficiency) / Thalassaemia / Thalassemia syndrome (disorder) / Mediterranean anemia (with other hemoglobinopathy) / Thalassaemia NOS / Thalassaemias / Thalassaemic disorders / Thalassemias / Thalassemia (disorder) / (Mediterranean anaemia) or (thalassaemia NOS) / Thalassemia NOS (disorder)

DrugDrug NameDrug Description
DB01609DeferasiroxAn iron chelator used to treat chronic iron overload caused by blood transfusions. Also used in patients with non-transfusion-dependent thalassemia syndromes, and in patients with elevated liver iron concentration and serum ferritin.
DrugDrug NamePhaseStatusCount
DB18646SLN1241Completed1
DB01609Deferasirox2Completed2
DB17692Vamifeport2Completed1
DB01609Deferasirox4Completed1