Severe Hemophilia B

Also known as: Severe Haemophilia B / Hemophilia B, Severe

DrugDrug NameDrug Description
DB16791Etranacogene dezaparvovecAn adeno-associated virus vector-based gene therapy used for the treatment of hemophilia B (congenital factor IX deficiency).
DB16783Fidanacogene elaparvovecFidanacogene elaparvovec is an adeno-associated viral (AAV) vector-based gene therapy indicated for the treatment of adults (aged 18 years or older) with moderately severe to severe Hemophilia B (congenital Factor...
DrugDrug NameTargetType