Metachromatic Leukodystrophy (MLD)

Also known as: Leukodystrophy, Metachromatic / Metachromatic Leukodystrophy / Other sphingolipidosis / Metachromatic leukodystrophy, juvenile type (disorder) / Metachromatic leucodystrophy (disorder)

DrugDrug NameDrug Description
DB17538Atidarsagene autotemcelA gene therapy comprising autologous CD34+ enriched stem cells encoding the human arylsulfatase A (ARSA) gene used to treat metachromatic leukodystrophy (MLD).
DrugDrug NamePhaseStatusCount
DB17671Recombinant human arylsulfatase A1 / 2Active Not Recruiting1
DB17671Recombinant human arylsulfatase A1 / 2Completed1
DB17644TAK-6111 / 2Active Not Recruiting1
DB17644TAK-6111 / 2Completed1
DB00087Alemtuzumab2Completed2
DB01008Busulfan2Completed1
DB00631Clofarabine2Completed1
DB06189Clofarabine2Completed1
DB00531Cyclophosphamide2Completed1
DB00091Cyclosporine2Completed1
DB01005Hydroxyurea2Completed1
DB01042Melphalan2Completed1
DB00688Mycophenolate mofetil2Completed1
DB17671Recombinant human arylsulfatase A2Active Not Recruiting1
DB17644TAK-6112Active Not Recruiting1
DB01008Busulfan2 / 3Completed1
DB00531Cyclophosphamide2 / 3Completed1
DB04974RimiducidNot AvailableNo Longer Available1
DB00682WarfarinNot AvailableCompleted1