Thalassemia Major (TM)

Also known as: Thalassemia Major / Beta thalassemia / Mediterranean anemia / Mediterranean anaemia / Cooley's anaemia / Thalassaemia major / Thalassemia major (disorder) / Homozygous beta thalassemia (disorder) / Cooley's anemia / Thalassemia, unspecified / Thalassemia / Thalassemia syndrome (disorder) / Thalassaemia NOS / Thalassaemic disorders / Thalassemia (disorder) / Thalassaemia

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB01281Abatacept1Completed1
DB06151Acetylcysteine1Not Yet Recruiting1
DB00151Cysteine1Completed1
DB01592Iron1Not Yet Recruiting1
DB00935Oxymetazoline1Not Yet Recruiting1
DB00928Azacitidine2Terminated1
DB01008Busulfan2Terminated1
DB01609Deferasirox2Completed1
DB06643Denosumab2Completed1
DB01073Fludarabine2Terminated1
DB11620Neridronic Acid2Completed1
DB12600Phenylbutyric acid2Terminated1
DB00635Prednisone2Terminated1
DB08877Ruxolitinib2Completed1
DB00864Tacrolimus2Terminated1
DB00381Amlodipine2 / 3Completed1
DB00126Ascorbic acid2 / 3Unknown Status1
DB08826Deferiprone2 / 3Unknown Status1
DB00746Deferoxamine2 / 3Completed1
DB14242Honey2 / 3Completed1
DB01005Hydroxyurea2 / 3Completed1
DB01592Iron2 / 3Unknown Status1
DB00098Antithymocyte immunoglobulin (rabbit)4Recruiting1
DB00098Antithymocyte immunoglobulin (rabbit)4Unknown Status1
DB00074Basiliximab4Recruiting1
DB00074Basiliximab4Unknown Status1
DB01008Busulfan4Recruiting1
DB01008Busulfan4Unknown Status1
DB00169Cholecalciferol4Unknown Status1
DB00531Cyclophosphamide4Recruiting1
DB00531Cyclophosphamide4Unknown Status1
DB00091Cyclosporine4Recruiting1
DB01609Deferasirox4Completed1
DB08826Deferiprone4Completed2
DB00746Deferoxamine4Completed3
DB01073Fludarabine4Recruiting1
DB01073Fludarabine4Unknown Status1
DB12281Luspatercept4Recruiting1
DB00563Methotrexate4Recruiting1
DB00563Methotrexate4Unknown Status1
DB00688Mycophenolate mofetil4Recruiting1
DB00688Mycophenolate mofetil4Unknown Status1
DB08877Ruxolitinib4Recruiting1
DB00864Tacrolimus4Recruiting1
DB00864Tacrolimus4Unknown Status1
DB01008BusulfanNot AvailableCompleted1
DB00531CyclophosphamideNot AvailableCompleted1