Genetic Diseases

Also known as: Genetics Disease / Genetic Disease / Genetic disease (disorder) / Hereditary disease (disorder) / Hereditary Diseases / Hereditary disorder NOS / Hereditary disorder

DrugDrug NameDrug Description
DB00052SomatotropinA recombinant human growth hormone used as replacement therapy in various conditions of growth failure, growth hormone deficiency, and weakness in children and adults.
DrugDrug NamePhaseStatusCount
DB15080ELX-021Completed2
DB15080ELX-021Terminated1
DB00531Cyclophosphamide2Terminated1
DB15080ELX-022Terminated1
DB17635Nedosiran2Completed1
DB01045Rifampicin2Recruiting1
DB11917Vatiquinone2Completed1
DB12159Dupilumab3Completed1
DB17635Nedosiran3Enrolling by Invitation1
DB00227Lovastatin4Completed1
DB01261Sitagliptin4Recruiting1