Sickle Cell Disorders

Also known as: Sickle Cell SC Disease / Sickle Cells Disease / Sickle Cell Disease (SCD) / Sickle-cell Disease (SCD) / Sickle-Cell Disease / Sickle Cell Disorder / Sickle Cell Disease / SC Disease / Sickle-cell disease without crisis / Sickle-cell anemia, unspecified / Sickle-cell anaemia, unspecified / Sickle-cell disorders / Sickle cell anaemia / Anaemia sickle cell / Sickle-cell anaemia / Sickle cell disease NOS / Sickling disorder due to hemoglobin S (disorder) / Sickle-cell anemia / Sickle cell anemia / Sickle cell-hemoglobin SS disease (disorder) / Anemia sickle cell / Anemia, Sickle Cell / Sickle-cell/Hb-C disease / Sickle-cell/Hb-C disease without crisis / Hemoglobin SC Disease / Sickle cell-hemoglobin C disease (disorder) / Sickle cell Hb-C disease / Haemoglobin SC disease / Hb-SC / Double heterozygous sickling disorders / Double heterozygous sickling disorder (disorder)

DrugDrug NameDrug Description
DB15271CrizanlizumabA monoclonal antibody that targets selectin to reduce the frequency of vasooclusive crises in patients with sickle cell disease.
DB15572Exagamglogene autotemcelAn autologous CRISPR-Cas9 modified hematopoietic stem cell therapy for the treatment of patients with sickle cell disease and recurrent vaso-occlusive crises.
DB01005HydroxyureaAn antimetabolite used to treat sickle cell anemia crisis, resistant chronic myeloid leukemia, and Locally advanced squamous cell carcinomas of the head and neck (excluding the lip).
DB18680Lovotibeglogene autotemcelAn autologous CD34+ cell therapy used to treat sickle cell disease by providing a functional copy of the beta-globin gene
DB09210PiracetamA nootropic cyclic GABA derivative used in myoclonus, sickle cell disease, alcohol dependence, and as a general cognitive enhancer.
DB14975VoxelotorA drug used to inhibit the polymerization of hemoglobin S, preventing the painful and sometimes lethal vaso-occlusive crises associated with sickle cell disease.
DrugDrug NamePhaseStatusCount
DB00087Alemtuzumab0Terminated1
DB00098Antithymocyte immunoglobulin (rabbit)0Withdrawn1
DB00121Biotin0Completed1
DB00188Bortezomib0Withdrawn1
DB16741Bortezomib D-mannitol0Withdrawn1
DB01008Busulfan0Withdrawn1
DB00531Cyclophosphamide0Withdrawn1
DB01234Dexamethasone0Withdrawn1
DB01073Fludarabine0Withdrawn1
DB01005Hydroxyurea0Completed1
DB01005Hydroxyurea0Recruiting1
DB00678Losartan0Completed1
DB00331Metformin0Completed1
DB16236Mitapivat0Completed1
DB00688Mycophenolate mofetil0Withdrawn1
DB00073Rituximab0Withdrawn1
DB00877Sirolimus0Terminated1
DB00864Tacrolimus0Withdrawn1
DB00624Testosterone0Withdrawn1
DB122985-Hydroxymethylfurfural1Completed1
DB01281Abatacept1Active Not Recruiting1
DB01281Abatacept1Completed1
DB00316Acetaminophen1Active Not Recruiting1
DB03128Acetylcholine1Completed1
DB00945Acetylsalicylic acid1Completed1
DB00087Alemtuzumab1Active Not Recruiting1
DB00087Alemtuzumab1Recruiting1
DB00087Alemtuzumab1Terminated1
DB00098Antithymocyte immunoglobulin (rabbit)1Active Not Recruiting2
DB15164Apadamtase alfa1Completed1
DB00207Azithromycin1Withdrawn1
DB00121Biotin1Recruiting1
DB01222Budesonide1Completed1
DB01156Bupropion1Completed1
DB06774Capsaicin1Completed1
DB00155Citrulline1Completed2
DB00155Citrulline1Unknown Status1
DB00155Citrulline1Withdrawn1
DB16128Crovalimab1Recruiting1
DB00531Cyclophosphamide1Active Not Recruiting1
DB00531Cyclophosphamide1Terminated1
DB00091Cyclosporine1Active Not Recruiting1
DB01262Decitabine1Completed1
DB01262Decitabine1Recruiting1
DB08826Deferiprone1Completed1
DB01075Diphenhydramine1Active Not Recruiting1
DB00470Dronabinol1Terminated1
DB00016Erythropoietin1Completed1
DB18176Etavopivat1Completed1
DB01073Fludarabine1Active Not Recruiting1
DB01073Fludarabine1Completed1
DB01073Fludarabine1Terminated1
DB00712Flurbiprofen1Completed1
DB12010Fostamatinib1Not Yet Recruiting1
DB00695Furosemide1Completed1
DB18229Hemopexin1Completed1
DB01005Hydroxyurea1Completed2
DB17860MP4CO1Completed1
DB01042Melphalan1Active Not Recruiting1
DB00454Meperidine1Active Not Recruiting1
DB00331Metformin1Completed1
DB00563Methotrexate1Active Not Recruiting1
DB00959Methylprednisolone1Active Not Recruiting1
DB14158Microcrystalline cellulose1Completed1
DB14158Microcrystalline cellulose1Terminated1
DB00683Midazolam1Completed2
DB01017Minocycline1Not Yet Recruiting1
DB14939Motixafortide1Recruiting1
DB00688Mycophenolate mofetil1Active Not Recruiting2
DB00688Mycophenolate mofetil1Terminated1
DB01024Mycophenolic acid1Active Not Recruiting1
DB17730NKTT-1201Completed1
DB00108Natalizumab1Recruiting1
DB02701Nicotinamide1Recruiting1
DB09112Nitrous acid1Completed1
DB00338Omeprazole1Completed1
DB05262Oxypurinol1Completed1
DB06603Panobinostat1Recruiting1
DB17720Pegylated carboxyhemoglobin (bovine)1Completed1
DB00552Pentostatin1Active Not Recruiting1
DB06809Plerixafor1Active Not Recruiting1
DB06809Plerixafor1Completed1
DB06809Plerixafor1Recruiting1
DB06209Prasugrel1Completed1
DB00571Propranolol1Terminated1
DB06213Regadenoson1Completed1
DB00912Repaglinide1Completed1
DB01098Rosuvastatin1Completed1
DB01001Salbutamol1Completed1
DB00877Sirolimus1Active Not Recruiting1
DB00877Sirolimus1Recruiting1
DB00877Sirolimus1Terminated1
DB09153Sodium chloride1Completed1
DB00864Tacrolimus1Active Not Recruiting2
DB12484Tetrahydrouridine1Completed1
DB12484Tetrahydrouridine1Recruiting1
DB04572Thiotepa1Active Not Recruiting1
DB08816Ticagrelor1Completed2
DB11815Tilarginine1Completed1
DB16193Tovinontrine1Completed1
DB14975Voxelotor1Completed4
DB09145Water1Completed1
DB00744Zileuton1Completed1
DB177062,2-Dimethylbutyrate1 / 2Completed1
DB01281Abatacept1 / 2Recruiting1
DB06151Acetylcysteine1 / 2Completed1
DB00087Alemtuzumab1 / 2Active Not Recruiting2
DB00087Alemtuzumab1 / 2Completed1
DB00087Alemtuzumab1 / 2Recruiting1
DB00125Arginine1 / 2Recruiting1
DB16367Autologous peripheral blood-derived CD34+ cells1 / 2Recruiting1
DB00207Azithromycin1 / 2Withdrawn1
DB12783Benserazide1 / 2Recruiting1
DB16900Betibeglogene autotemcel1 / 2Completed1
DB18136Briquilimab1 / 2Recruiting1
DB01008Busulfan1 / 2Active Not Recruiting1
DB00169Cholecalciferol1 / 2Completed1
DB00318Codeine1 / 2Completed1
DB15271Crizanlizumab1 / 2Not Yet Recruiting1
DB00531Cyclophosphamide1 / 2Active Not Recruiting1
DB00091Cyclosporine1 / 2Completed1
DB00746Deferoxamine1 / 2Withdrawn1
DB03756Doconexent1 / 2Terminated1
DB00063Eptifibatide1 / 2Terminated1
DB00016Erythropoietin1 / 2Recruiting1
DB18176Etavopivat1 / 2Recruiting1
DB13961Fish oil1 / 2Terminated1
DB01073Fludarabine1 / 2Completed2
DB11242Gelatin1 / 2Terminated1
DB00028Human immunoglobulin G1 / 2Recruiting1
DB01005Hydroxyurea1 / 2Active Not Recruiting2
DB01005Hydroxyurea1 / 2Completed1
DB01005Hydroxyurea1 / 2Recruiting1
DB01005Hydroxyurea1 / 2Terminated1
DB00159Icosapent1 / 2Terminated1
DB00619Imatinib1 / 2Recruiting1
DB14009Medical Cannabis1 / 2Completed1
DB01042Melphalan1 / 2Completed1
DB16236Mitapivat1 / 2Active Not Recruiting1
DB00688Mycophenolate mofetil1 / 2Completed1
DB09112Nitrous acid1 / 2Terminated1
DB00552Pentostatin1 / 2Active Not Recruiting1
DB06809Plerixafor1 / 2Active Not Recruiting1
DB12544Rivipansel1 / 2Completed1
DB00641Simvastatin1 / 2Completed2
DB00641Simvastatin1 / 2Unknown Status1
DB00877Sirolimus1 / 2Active Not Recruiting2
DB00877Sirolimus1 / 2Recruiting1
DB00864Tacrolimus1 / 2Completed1
DB04572Thiotepa1 / 2Completed1
DB11094Vitamin D1 / 2Completed1
DB14975Voxelotor1 / 2Recruiting1
DB00399Zoledronic acid1 / 2Withdrawn1
DB177062,2-Dimethylbutyrate2Completed1
DB177062,2-Dimethylbutyrate2Terminated1
DB122985-Hydroxymethylfurfural2Terminated1
DB00054Abciximab2Withdrawn1
DB03128Acetylcholine2Completed1
DB00087Alemtuzumab2Active Not Recruiting1
DB00087Alemtuzumab2Completed3
DB00087Alemtuzumab2Recruiting4
DB00087Alemtuzumab2Suspended1
DB00087Alemtuzumab2Terminated1
DB00630Alendronic acid2Not Yet Recruiting1
DB11118Ammonia2Recruiting1
DB09312Antilymphocyte immunoglobulin (horse)2Completed2
DB00098Antithymocyte immunoglobulin (rabbit)2Active Not Recruiting1
DB00098Antithymocyte immunoglobulin (rabbit)2Completed2
DB00098Antithymocyte immunoglobulin (rabbit)2Recruiting2
DB00098Antithymocyte immunoglobulin (rabbit)2Terminated2
DB00125Arginine2Completed1
DB01076Atorvastatin2Completed1
DB00993Azathioprine2Suspended1
DB11105Benzalkonium2Recruiting1
DB00188Bortezomib2Recruiting1
DB00921Buprenorphine2Completed1
DB01008Busulfan2Active Not Recruiting1
DB01008Busulfan2Completed5
DB01008Busulfan2Terminated1
DB16798Cevaretigene ritoparvovec2Completed1
DB00169Cholecalciferol2Active Not Recruiting1
DB00169Cholecalciferol2Completed2
DB09110Coenzyme M2Active Not Recruiting1
DB15271Crizanlizumab2Completed2
DB15271Crizanlizumab2Recruiting1
DB16128Crovalimab2Recruiting1
DB00531Cyclophosphamide2Active Not Recruiting2
DB00531Cyclophosphamide2Completed3
DB00531Cyclophosphamide2Recruiting3
DB00531Cyclophosphamide2Suspended1
DB00531Cyclophosphamide2Terminated3
DB06779Dalteparin2Completed1
DB01262Decitabine2Completed1
DB01262Decitabine2Recruiting1
DB01609Deferasirox2Completed3
DB00746Deferoxamine2Completed1
DB04932Defibrotide2Completed1
DB04932Defibrotide2Recruiting1
DB01234Dexamethasone2Recruiting1
DB03756Doconexent2Unknown Status1
DB00470Dronabinol2Recruiting1
DB18100Epeleuton2Recruiting1
DB18176Etavopivat2Not Yet Recruiting1
DB18176Etavopivat2Recruiting2
DB00813Fentanyl2Withdrawn1
DB00099Filgrastim2Completed1
DB01073Fludarabine2Active Not Recruiting3
DB01073Fludarabine2Completed5
DB01073Fludarabine2Recruiting3
DB01073Fludarabine2Terminated2
DB01073Fludarabine2Unknown Status1
DB00996Gabapentin2Completed1
DB01109Heparin2Terminated1
DB15726Human Umbilical Cord Mesenchymal Stem Cells2Completed1
DB00327Hydromorphone2Withdrawn1
DB01005Hydroxyurea2Active Not Recruiting1
DB01005Hydroxyurea2Completed5
DB01005Hydroxyurea2Recruiting4
DB01005Hydroxyurea2Suspended1
DB01005Hydroxyurea2Terminated1
DB01050Ibuprofen2Withdrawn1
DB12665Isoquercetin2Completed1
DB12665Isoquercetin2Withdrawn1
DB16403Isoquercitrin2Completed1
DB01221Ketamine2Completed1
DB01221Ketamine2Terminated1
DB00130L-Glutamine2Completed1
DB01202Levetiracetam2Terminated1
DB00281Lidocaine2Not Yet Recruiting1
DB00678Losartan2Recruiting1
DB00678Losartan2Terminated1
DB17860MP4CO2Withdrawn1
DB08932Macitentan2Terminated1
DB14009Medical Cannabis2Recruiting1
DB01042Melphalan2Completed2
DB01042Melphalan2Recruiting1
DB01042Melphalan2Unknown Status1
DB01043Memantine2Unknown Status1
DB00563Methotrexate2Completed1
DB16236Mitapivat2Not Yet Recruiting1
DB00764Mometasone2Completed1
DB14512Mometasone furoate2Completed1
DB00295Morphine2Withdrawn1
DB00688Mycophenolate mofetil2Recruiting2
DB00688Mycophenolate mofetil2Terminated2
DB00688Mycophenolate mofetil2Unknown Status1
DB01183Naloxone2Completed1
DB00627Niacin2Completed1
DB00435Nitric Oxide2Completed1
DB00435Nitric Oxide2Terminated2
DB09112Nitrous acid2Completed1
DB06690Nitrous oxide2Terminated1
DB15238Olinciguat2Completed1
DB09140Oxygen2Terminated1
DB00552Pentostatin2Recruiting1
DB06809Plerixafor2Suspended1
DB06809Plerixafor2Terminated1
DB06809Plerixafor2Withdrawn1
DB06209Prasugrel2Completed1
DB00571Propranolol2Completed1
DB06213Regadenoson2Recruiting1
DB01220Rifaximin2Completed1
DB01220Rifaximin2Unknown Status1
DB08931Riociguat2Completed1
DB00073Rituximab2Recruiting1
DB00073Rituximab2Terminated1
DB12544Rivipansel2Completed1
DB00936Salicylic acid2Terminated1
DB00360Sapropterin2Completed1
DB06280Senicapoc2Completed1
DB15007Sevuparin2Completed1
DB00203Sildenafil2Completed1
DB00203Sildenafil2Terminated1
DB00877Sirolimus2Completed1
DB00877Sirolimus2Recruiting4
DB00877Sirolimus2Suspended1
DB00877Sirolimus2Terminated2
DB00877Sirolimus2Unknown Status1
DB09153Sodium chloride2Withdrawn1
DB09422Soybean oil2Unknown Status1
DB14546Sulfate ion2Not Yet Recruiting1
DB00864Tacrolimus2Completed1
DB00864Tacrolimus2Recruiting1
DB00864Tacrolimus2Terminated1
DB12484Tetrahydrouridine2Recruiting1
DB04572Thiotepa2Active Not Recruiting1
DB04572Thiotepa2Completed2
DB04572Thiotepa2Suspended1
DB08816Ticagrelor2Completed1
DB11815Tilarginine2Completed1
DB06273Tocilizumab2Recruiting1
DB16193Tovinontrine2Active Not Recruiting1
DB16193Tovinontrine2Completed1
DB16193Tovinontrine2Terminated1
DB17692Vamifeport2Active Not Recruiting1
DB05737Varespladib methyl2Terminated1
DB11094Vitamin D2Completed1
DB02546Vorinostat2Terminated1
DB14975Voxelotor2Active Not Recruiting1
DB14975Voxelotor2Completed1
DB14975Voxelotor2Recruiting1
DB14975Voxelotor2Terminated1
DB01593Zinc2Not Yet Recruiting1
DB00087Alemtuzumab2 / 3Completed1
DB00098Antithymocyte immunoglobulin (rabbit)2 / 3Completed1
DB01008Busulfan2 / 3Completed1
DB00608Chloroquine2 / 3Unknown Status1
DB00531Cyclophosphamide2 / 3Completed1
DB01609Deferasirox2 / 3Unknown Status1
DB08826Deferiprone2 / 3Unknown Status1
DB00746Deferoxamine2 / 3Unknown Status1
DB18176Etavopivat2 / 3Recruiting1
DB15572Exagamglogene autotemcel2 / 3Active Not Recruiting1
DB00927Famotidine2 / 3Recruiting1
DB00099Filgrastim2 / 3Completed1
DB01073Fludarabine2 / 3Completed1
DB00158Folic acid2 / 3Completed1
DB00653Magnesium sulfate2 / 3Completed1
DB16236Mitapivat2 / 3Recruiting1
DB00295Morphine2 / 3Completed1
DB00435Nitric Oxide2 / 3Completed1
DB11133Omega-3 fatty acids2 / 3Completed1
DB00641Simvastatin2 / 3Completed1
DB03904Urea2 / 3Completed1
DB09322Zinc sulfate2 / 3Completed1
DB06151Acetylcysteine3Completed1
DB00945Acetylsalicylic acid3Recruiting1
DB00087Alemtuzumab3Completed1
DB06605Apixaban3Terminated1
DB00125Arginine3Completed1
DB00125Arginine3Recruiting2
DB15271Crizanlizumab3Active Not Recruiting1
DB01609Deferasirox3Completed1
DB03756Doconexent3Unknown Status1
DB15572Exagamglogene autotemcel3Enrolling by Invitation1
DB15572Exagamglogene autotemcel3Not Yet Recruiting1
DB15572Exagamglogene autotemcel3Recruiting2
DB01073Fludarabine3Completed1
DB00327Hydromorphone3Terminated1
DB01005Hydroxyurea3Completed4
DB01005Hydroxyurea3Recruiting2
DB12246Inclacumab3Active Not Recruiting1
DB12246Inclacumab3Completed1
DB12246Inclacumab3Recruiting1
DB01221Ketamine3Recruiting1
DB01221Ketamine3Unknown Status1
DB01221Ketamine3Withdrawn1
DB01042Melphalan3Completed1
DB00422Methylphenidate3Completed1
DB00295Morphine3Completed1
DB00295Morphine3Terminated1
DB00844Nalbuphine3Completed1
DB11333Poloxamer 1883Completed2
DB06209Prasugrel3Terminated1
DB06228Rivaroxaban3Recruiting1
DB12544Rivipansel3Terminated1
DB12778Rivipansel3Terminated1
DB06280Senicapoc3Terminated2
DB09422Soybean oil3Unknown Status1
DB08816Ticagrelor3Terminated1
DB08816Ticagrelor3Withdrawn1
DB14975Voxelotor3Active Not Recruiting3
DB14975Voxelotor3Completed1
DB14975Voxelotor3Recruiting1
DB14975Voxelotor3Terminated1
DB00173Adenine4Completed1
DB00575Clonidine4Recruiting1
DB00318Codeine4Withdrawn1
DB15271Crizanlizumab4Completed1
DB15271Crizanlizumab4Recruiting1
DB01609Deferasirox4Completed1
DB08826Deferiprone4Terminated2
DB00746Deferoxamine4Completed1
DB00746Deferoxamine4Terminated1
DB00514Dextromethorphan4Withdrawn1
DB01452Diamorphine4Terminated1
DB00294Etonogestrel4Completed1
DB00294Etonogestrel4Recruiting1
DB00813Fentanyl4Completed1
DB00327Hydromorphone4Completed1
DB01005Hydroxyurea4Completed3
DB01050Ibuprofen4Terminated1
DB04335Inosine4Completed1
DB01221Ketamine4Terminated1
DB00130L-Glutamine4Completed2
DB00583Levocarnitine4Completed1
DB00295Morphine4Completed2
DB00295Morphine4Recruiting1
DB00295Morphine4Terminated1
DB00295Morphine4Withdrawn1
DB11194Pyruvic acid4Completed1
DB14504Sodium phosphate, dibasic, unspecified form4Completed1
DB09449Sodium phosphate, monobasic4Completed1
DB09525Sodium phosphate, monobasic4Completed1
DB00163Vitamin E4Completed1
DB14975Voxelotor4Active Not Recruiting1
DB14975Voxelotor4Completed1
DB00819AcetazolamideNot AvailableCompleted1
DB00819AcetazolamideNot AvailableUnknown Status1
DB00092AlefaceptNot AvailableTerminated1
DB00087AlemtuzumabNot AvailableRecruiting1
DB00087AlemtuzumabNot AvailableTerminated1
DB00098Antithymocyte immunoglobulin (rabbit)Not AvailableActive Not Recruiting1
DB01008BusulfanNot AvailableTerminated1
DB09157Carbon dioxideNot AvailableRecruiting1
DB00169CholecalciferolNot AvailableCompleted1
DB00631ClofarabineNot AvailableCompleted1
DB09110Coenzyme MNot AvailableActive Not Recruiting1
DB09110Coenzyme MNot AvailableTerminated1
DB15271CrizanlizumabNot AvailableAvailable1
DB00531CyclophosphamideNot AvailableActive Not Recruiting1
DB00531CyclophosphamideNot AvailableTerminated1
DB01234DexamethasoneNot AvailableRecruiting1
DB09341Dextrose, unspecified formNot AvailableTerminated1
DB00584EnalaprilNot AvailableTerminated1
DB01073FludarabineNot AvailableActive Not Recruiting1
DB01073FludarabineNot AvailableCompleted2
DB00158Folic acidNot AvailableCompleted1
DB11627Hepatitis B Vaccine (Recombinant)Not AvailableRecruiting1
DB01005HydroxyureaNot AvailableActive Not Recruiting1
DB01005HydroxyureaNot AvailableCompleted5
DB01005HydroxyureaNot AvailableRecruiting2
DB14444Influenza A virus A/California/7/2009 (H1N1)-like antigen (propiolactone inactivated)Not AvailableCompleted1
DB01221KetamineNot AvailableTerminated1
DB01221KetamineNot AvailableUnknown Status1
DB01042MelphalanNot AvailableCompleted1
DB00333MethadoneNot AvailableCompleted1
DB00295MorphineNot AvailableCompleted1
DB00688Mycophenolate mofetilNot AvailableActive Not Recruiting1
DB00417PhenoxymethylpenicillinNot AvailableCompleted1
DB01131ProguanilNot AvailableCompleted1
DB06213RegadenosonNot AvailableUnknown Status1
DB00877SirolimusNot AvailableActive Not Recruiting1
DB04572ThiotepaNot AvailableCompleted1
DB11300ThrombinNot AvailableRecruiting1
DB11094Vitamin DNot AvailableCompleted1
DB14975VoxelotorNot AvailableAvailable1
DB14975VoxelotorNot AvailableCompleted1
DB14975VoxelotorNot AvailableNo Longer Available1
DB14975VoxelotorNot AvailableRecruiting2