Severe Combined Immunodeficiency Disease, X-linked

Also known as: X Linked Combined Immunodeficiency / XSCID / SCID, X Linked / X-Linked Severe Combined Immune Deficiency (XSCID) / X-linked Severe Combined Immunodeficiency (XSCID) / X-linked Severe Combined Immunodeficiency / Severe Combined Immunodeficiency, X-Linked / X linked severe combined immunodeficiency / Severe Combined Immunodeficiency, X Linked / SCID-X1 / X-Linked Combined Immunodeficiency Diseases / Combined immunodeficiency, unspecified / Combined immunodeficiency / Combined immunodeficiency syndrome / Combined immunity deficiency / Combined immunodeficiencies / Combined immunodeficiency disease (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB16367Autologous peripheral blood-derived CD34+ cells1Recruiting1
DB00091Cyclosporine1Completed1
DB00688Mycophenolate mofetil1Completed1
DB01008Busulfan1 / 2Recruiting1
DB01008Busulfan1 / 2Suspended1
DB01277Mecasermin1 / 2Terminated1
DB00039Palifermin1 / 2Recruiting1