Pompe Disease (Infantile-Onset)

Also known as: Pompe Disease Infantile-Onset / Infantile-onset Pompe Disease

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB01272Alglucosidase alfa1Recruiting1
DB09051Elosulfase alfa1Recruiting1
DB01279Galsulfase1Recruiting1
DB01271Idursulfase1Recruiting1
DB00090Laronidase1Recruiting1
DB11563Sebelipase alfa1Recruiting1
DB12366Vestronidase alfa1Recruiting1
DB01272Alglucosidase alfa2Completed1
DB01272Alglucosidase alfa4Terminated1
DB16708Cipaglucosidase alfaNot AvailableAvailable1
DB00419MiglustatNot AvailableAvailable1