Krabbe's Disease

Also known as: Krabbe Disease / Galactosylceramide beta-galactosidase deficiency (disorder) / Galactosylceramide lipidosis / Globoid cell leukodystrophy, early onset (disorder) / Leukodystrophy, Globoid Cell

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB18340FBX-1011 / 2Active Not Recruiting1
DB18340FBX-1011 / 2Recruiting1
DB00087Alemtuzumab2Completed1
DB00087Alemtuzumab2Terminated1
DB01008Busulfan2Completed1
DB01008Busulfan2Terminated1
DB00531Cyclophosphamide2Completed1
DB00531Cyclophosphamide2Terminated1
DB00091Cyclosporine2Completed1
DB00688Mycophenolate mofetil2Completed1