Phenylketonuria (PKU)
Also known as: Phenylketonurias / Pku Phenylketonuria / PKU / Phenylketonuria / Phenylalaninaemia / Phenylalaninemia / Classical phenylketonuria / Classical phenylketonuria (disorder) / Phenylketonuria I / Phenylpyruvic oligophrenia
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB17684 | HMI-103 | 1 | Terminated | 1 |
| DB00218 | Moxifloxacin | 1 | Completed | 1 |
| DB12839 | Pegvaliase | 1 | Completed | 1 |
| DB00360 | Sapropterin | 1 | Completed | 1 |
| DB00360 | Sapropterin | 1 | Terminated | 1 |
| DB16810 | Domofenogene zalfaparvovec | 1 / 2 | Active Not Recruiting | 1 |
| DB11118 | Ammonia | 2 | Completed | 2 |
| DB17618 | Labafenogene marselecobac | 2 | Completed | 1 |
| DB12839 | Pegvaliase | 2 | Completed | 4 |
| DB00120 | Phenylalanine | 2 | Completed | 2 |
| DB00360 | Sapropterin | 2 | Completed | 3 |
| DB00360 | Sapropterin | 2 | Terminated | 2 |
| DB09255 | Dextran | 3 | Completed | 1 |
| DB12839 | Pegvaliase | 3 | Active Not Recruiting | 1 |
| DB12839 | Pegvaliase | 3 | Completed | 3 |
| DB00360 | Sapropterin | 3 | Completed | 8 |
| DB16326 | Sepiapterin | 3 | Not Yet Recruiting | 1 |
| DB16326 | Sepiapterin | 3 | Recruiting | 1 |
| DB00360 | Sapropterin | 4 | Completed | 4 |
| DB00360 | Sapropterin | 4 | Unknown Status | 1 |
| DB12839 | Pegvaliase | Not Available | Completed | 1 |
| DB12839 | Pegvaliase | Not Available | Enrolling by Invitation | 1 |
| DB12839 | Pegvaliase | Not Available | Recruiting | 3 |
| DB00360 | Sapropterin | Not Available | Approved for Marketing | 1 |
| DB00360 | Sapropterin | Not Available | Completed | 7 |
| DB00360 | Sapropterin | Not Available | Terminated | 3 |
| DB00360 | Sapropterin | Not Available | Withdrawn | 1 |