IPEX

Also known as: Immunodysregulation Polyendocrinopathy Enteropathy X-linked Syndrome / IPEX syndrome / Insulin-dependent diabetes mellitus secretory diarrhea syndrome (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00087Alemtuzumab2Recruiting1
DB01073Fludarabine2Recruiting1
DB01042Melphalan2Recruiting1
DB04572Thiotepa2Recruiting1