Mucopolysaccharidosis Type 7

Also known as: MPS VII / Mucopolysaccharidosis Type VII / Mucopolysaccharidosis VII / Other mucopolysaccharidoses / Mucopolysaccharidosis, MPS-VII (disorder) / Deficiency of beta-glucuronidase (disorder) / Sly's syndrome

DrugDrug NameDrug Description
DB12366Vestronidase alfaA recombinant beta-glucuronidase used to treat mucopolysaccharidosis VII.
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB01272Alglucosidase alfa1Recruiting1
DB09051Elosulfase alfa1Recruiting1
DB01279Galsulfase1Recruiting1
DB01271Idursulfase1Recruiting1
DB00090Laronidase1Recruiting1
DB11563Sebelipase alfa1Recruiting1
DB12366Vestronidase alfa1Recruiting1
DB12366Vestronidase alfa1 / 2Completed1
DB12366Vestronidase alfa2Completed1
DB12366Vestronidase alfa3Completed2
DB12366Vestronidase alfaNot AvailableAvailable1
DB12366Vestronidase alfaNot AvailableNo Longer Available1